Watch: World First: US Baby Treated With Personalized CRISPR Gene-Editing
When KJ Muldoon was just days old, his future seemed heartbreakingly uncertain. Diagnosed with a rare and often fatal genetic disorder, his options were limited to a liver transplant or an untested gene-editing treatment. His parents chose the unknown. That decision has now made KJ the first person in history to receive a fully personalized Crispr-based gene therapy—an infusion tailored to his exact mutation. It’s a breakthrough not just for him, but potentially for thousands with rare genetic diseases that have long defied treatment. Rob Stein with NPR has the full story, or watch the recap from The Children’s Hospital of Philadelphia below.
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